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Authors
Keyzor, Ian
Martins, Ana Maria
Uçar, Sema Kalkan
Yamakawa, Hiroyuki
Chien, Yin-Hsiu
Arslan, Nur
Niu, Dau-Ming
Tümer, Leyla
Baldock, Laura
Shohet, Simon
Giuliano, Joseph D.
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Funding
Funding for this research was provided by:
Amicus Therapeutics (Amicus Therapeutics)
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Article History
Received: 28 February 2024
Accepted: 29 March 2025
First Online: 11 August 2025
Declarations
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: This study was designed and monitored in accordance with the ethical principles of Good Clinical Practice guidelines and the Declaration of Helsinki. The clinical study protocol was reviewed and approved by the appropriate independent ethics committee or institutional review board at each study site.
: Not applicable.
: IK: was an employee of Amicus Therapeutics, Ltd. at the time of the study and holds stocks and shares in Amicus Therapeutics, Inc. JDG: Is an employee of Amicus Therapeutics, Inc. and holds stocks and shares in Amicus Therapeutics, Inc. SS: Is an employee of Amicus Therapeutics, Ltd. and holds stocks and shares in Amicus Therapeutics, Inc. LB: Employee of OPEN Health at the time of the study.
