Cheema, Ikreet
Goodwin, Jacob
Liewluck, Teerin
Bucelli, Robert Charles
Pestronk, Alan
Milone, Margherita https://orcid.org/0000-0002-4338-9007
Article History
Received: 20 March 2025
Accepted: 5 June 2025
First Online: 22 June 2025
Declarations
:
: The study was approved by the Mayo Clinic Institutional Review Board.
: Not applicable.
: Dr. Ikreet Cheema, Dr. Jacob Goodwin, Dr. Teerin Liewluck: Reports no disclosures. Dr. Robert Bucelli: Site PI for trials sponsored by Biogen MA, Ionis, and QurAlis. Paid consultant for Biogen MA. Honorarium from LGMD Masterclass. Advisory Boards for Regeneron and Biogen MA Inc. PI for the Mitchell and Friends Foundation Research Fund. Equity in Neuroquestions.com. Dr. Alan Pestronk: Reports no disclosures. Dr. Margherita Milone: Receives funding for the Muscular Dystrophy Association (MDA Care Center grant 497263).