Ferren, Edwin
Hillman, Paul R.
Kritzer, Amy
Ray, Joseph
Serrano, Alvaro
Northrup, Hope
Roberts, Paige
Dutta, Rana
Pramparo, Tiziano
Vig, Pamela
Steiner, Robert D.
Article History
Received: 23 December 2024
Accepted: 9 July 2025
First Online: 28 July 2025
Declarations
:
: Not applicable.
: Not applicable.
: EF and PRH are consultants for Mirum Pharmaceuticals, Inc. They were not compensated for the work on this manuscript. AK, JR, AS, and HN have no conflicts of interest to report. PR is a consultant for Mirum Pharmaceuticals, Inc. and has been a consultant for Vitaflo, PTC, Jnana, and Zevra. She was not compensated for the work on this manuscript. RD, TP, and PV are employees of and shareholders in Mirum Pharmaceuticals, Inc. RDS has been a consultant for Exact Sciences, Mirum Pharmaceuticals, Inc., PTC, and Ultragenyx. He has equity in Exact Sciences. He was not compensated for the work on this manuscript.