Blin, Mélanie
Tardieu, Marine
Lacombe, Didier
Gorce, Magali
Damaj, Léna
Barth, Magalie
Genevaz, Delphine
Vibet, Sophie
Labarthe, François https://orcid.org/0000-0001-9788-9667
Article History
Received: 15 April 2024
Accepted: 23 September 2025
First Online: 12 November 2025
Declarations
:
: Informed consent was obtained from each patient and their parents. Patients or their parents who refused to participate were not included. The study was approved by the local Ethics Committee in Human Research of the University Hospital of Tours (Ref. RNIPH21-AIE D MPS).
: Not applicable.
: DL reports personal fees from Sanofi-Genzyme, FL reports consulting fees from AlfaSigma, Biomarin and Sanofi-Genzyme, all of which are outside the submitted work; all the other authors declare no conflicts of interest with this work.