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Authors
MartÃ, Yasmina https://orcid.org/0000-0002-9057-8599
Gorni, Ksenija
Kumari, Sandhya
Mahajan, Anadi
Baranello, Giovanni
Waele, Liesbeth De
McGrattan, Katlyn E.
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Article History
Received: 18 July 2025
Accepted: 25 October 2025
First Online: 8 January 2026
Declarations
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: Ethical approval was not required for this study as data used in our analyses were obtained from publicly available published data.
: Not applicable.
: YM and KG are employed by, and own stock in, F. Hoffmann-La Roche Ltd. SK and AM were employed as consultants to F. Hoffmann-La Roche Ltd. GB has received speaker and consultancy honoraria from AveXis, F. Hoffmann-La Roche Ltd, PTC Therapeutics, and Sarepta Therapeutics. He has received fees for serving on advisory boards and has received equipment for indirect calorimetry to University College London from F. Hoffmann-La Roche Ltd. LDW has received honoraria for participating in advisory boards and/or symposia by Novartis, Biogen, and F. Hoffmann-La Roche Ltd. Her institution receives funding for clinical research and educative events from Biogen, Novartis, Scholar Rock, BioHaven, and F. Hoffmann-La Roche Ltd. LDW is a member of the European Reference Network for Rare Neuromuscular Diseases (ERN EURO-NMD). KEM has received honoraria for participating in advisory boards and/or symposia by Novartis and F. Hoffmann-La Roche Ltd. She has received funding for clinical research by Biogen and F. Hoffmann-La Roche Ltd.
