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Authors
Mistry, Pramod K. https://orcid.org/0000-0003-3447-6421
Carwile, Jenny L.
Burrow, Thomas Andrew
Tantawy, Azza Abdel Gawad
Camelo, Jose Simon
Ganesh, Jaya
Batsu, Isabela
Perichon, Maria Gabriela
Oliveira-dos-Santos, Antonio
Batista, Julie L.
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Article History
Received: 7 August 2025
Accepted: 13 February 2026
First Online: 11 March 2026
Declarations
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: Approval of the Registry data collection process at participating institutions includes institutional review boards or ethics committees and patient informed consent, as dictated by local policies.
: Not applicable. This manuscript does not contain any individual person’s data.
: Pramod K. Mistry was a principal investigator on the Sanofi-sponsored ENGAGE clinical trial of eliglustat, has received research and travel support from Sanofi. Thomas Andrew Burrow has received research funding, travel reimbursement, and payment for advisory services from Sanofi and Takeda. Azza Abdel Gawad Tantawy has received honoraria for participating as consultant in speakers’ bureau and advisory boards from Sanofi. Jose Simon Camelo has received honoraria for consultation and advisory board participation from Sanofi, and has received educational and travel support from Sanofi. Jaya Ganesh has received research funding, honoraria and travel support from Sanofi. Jenny L. Carwile, Isabela Batsu, Maria Gabriela Perichon, Antonio Oliveira-dos-Santos, and Julie L. Batista are Sanofi employees and may hold stock in the company.
