Donati, Maria Alice
Pasquini, Elisabetta
Spada, Marco
Polo, Giulia
Burlina, Alberto
Article History
Received: 28 May 2019
Accepted: 28 May 2019
First Online: 11 June 2019
Competing interests
: MAD has received speaker honoraria and travel support from Sanofi Genzyme, Biomarin, Shire and Actelion. The pilot project of NBS in Tuscany and Umbria has been partially supported by Sanofi Genzyme. AB has received speaker honoraria and travel support from Sanofi Genzyme, Biomarin, and Actelion. The remaining authors declare that they have no competing interests.