Caballero, Teresa
,
Zanichelli, Andrea
Aberer, Werner
Maurer, Marcus
Longhurst, Hilary J.
Bouillet, Laurence
Andresen, Irmgard
Funding for this research was provided by:
Shire Human Genetic Therapies
Article History
Received: 19 December 2017
Accepted: 28 February 2018
First Online: 23 March 2018