Keeley, Olivia
Mendoza, Emma
Menon, Druv
Coyne, Alyssa N.
Funding for this research was provided by:
National Institute of Neurological Disorders and Stroke (R01NS132836)
National Institute of Aging (R00NS123242)
Robert Packard Center for ALS Research, Johns Hopkins University
Muscular Dystrophy Association
BrightFocus Foundation
Article History
Received: 11 November 2024
Accepted: 13 December 2024
First Online: 21 December 2024
Declarations
:
: Not applicable.
: Not applicable.
: ANC has patents pending on (1) knockdown of CHMP7 (ASO, siRNA, protein degradation), (2) knockdown of SUN1 (ASO, siRNA), (3) knockdown of CHMP2B (ASO, siRNA), and (4) overexpression of POM121 to repair NPC injury cascades in ALS and dementia.