12 year follow up of enzyme-replacement therapy in two siblings with attenuated mucopolysaccharidosis I: the important role of early treatment
Crossref DOI link: https://doi.org/10.1186/s12881-016-0284-4
Published Online: 2016-03-10
Published Print: 2016-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Gabrielli, Orazio
Clarke, Lorne A.
Ficcadenti, Anna
Santoro, Lucia
Zampini, Lucia
Volpi, Nicola
Coppa, Giovanni V.