Funding for this research was provided by:
BioMarin Pharmaceutical ((Support por publication fee if manuscript is accepted))
Received: 15 March 2019
Accepted: 11 February 2020
First Online: 19 February 2020
Ethics approval and consent to participate
: The patient was studied as part of a research protocol approved by the local Ethics Committee (139.728 – CAPPesq - Comissão de Ética para Análise de Projetos de Pesquisa). The patient’s legal guardians (parents) have signed informed consent to participate in this study.
: The authors declare that they have no competing interests.