Funding for this research was provided by:
stichting spieren voor spieren (SvS2019001)
stichting voor sara (not applicable)
stichting stofwisselkracht (2018-15)
Received: 23 June 2021
Accepted: 27 July 2021
First Online: 12 August 2021
: This study is performed in accordance with the Declaration of Helsinki and has been approved by the medical ethical reviewing committee of Region Arnhem-Nijmegen (NL-number NL64269.091.17, dossier number 2017–3911; date of approval of last amendment: 8 July 2020). From all patients, or in case of children their parents or legal guardian, written informed consent will be obtained for participating in our study.
: Not applicable.
: Professor Jan A.M. Smeitink is Chief Executive Officer of Khondrion. All other authors declare that they have no competing interests.