Stettner, Georg M.
Hasselmann, Oswald
Tscherter, Anne
Galiart, Elea
Jacquier, David
Klein, Andrea
Article History
Received: 26 November 2022
Accepted: 20 February 2023
First Online: 28 February 2023
Declarations
:
: For this study data collected within the Swiss registry for Neuromuscular Disorders (Swiss-Reg-NMD) was used. This registry is hosted at the Institute of Social and Preventive Medicine (ISPM), University of Bern, Switzerland, since 2017 and was approved by the Cantonal Ethics Committee of Bern (20.06.2018, KEK Bern, 2018-00289). Parents provided written informed consent for the participation of their children in the Swiss-Reg-NMD. All methods were carried out in accordance with relevant guidelines and regulation. The research has been performed in accordance with the Declaration of Helsinki.
: Not applicable.
: GMS served on advisory boards of AveXis, Biogen, Novartis Gene Therapies and Roche.OH served on advisory boards of Biogen and Novartis Gene Therapies; he received speaker’s honoraria from Biogen. DJ served on advisory boards of AveXis, Biogen, Novartis Gene Therapies and Roche; he received speaker’s honoraria from Biogen and Roche, and a research grant from AveXis, Biogen and Roche. AT is employee of the Swiss-Reg-NMD.EG has no conflict of interest to report. AK served on advisory boards of AveXis, Biogen, Novartis Gene Therapies, Roche, Sarepta and Pfizer; she received speaker’s honoraria from Roche, Biogen, Pfizer and Novartis Gene Therapies.The Swiss-Reg-NMD is funded by ‘Schweizerische Muskelgesellschaft’, ‘Association Suisse Romande Intervenant contre les Maladies neuro-Musculaires’, ‘Associazione Malattie Genetiche Rare Svizzera italiana’, ‘SMA Schweiz’, ‘Duchenne Schweiz’ ‘Schweizerische Stiftung für die Erforschung der Muskelkrankheiten’ FSRMM; and receives unconditional and research grants from PTC Therapeutics lnternational, Sarepta International, Pfizer Switzerland, AveXis EU Limited, Roche Pharma Schweiz, Novartis Gene Therapies, and Biogen Switzerland AG. None of the funders was involved in the study design, data collection, analysis, interpretation of data or writing the article.