Llerena, Juan Jr
Kim, Chong Ae
Fano, Virginia
Rosselli, Pablo
Collett-Solberg, Paulo Ferrez
de Medeiros, Paula Frassinetti Vasconcelos
del Pino, Mariana
Bertola, Débora
Lourenço, Charles Marques
Cavalcanti, Denise Pontes
Félix, Têmis Maria
Rosa-Bellas, Antonio
Rossi, Norma Teresa
Cortes, Fanny
Abreu, Flávia
Cavalcanti, Nicolette
Ruz, Maria Cecilia Hervias
Baratela, Wagner
Article History
Received: 8 December 2021
Accepted: 15 July 2022
First Online: 19 August 2022
Declarations
:
: Not applicable.
: Not applicable.
: CAK, DB and NC received travel grant from BioMarin.VF, PR, MDP, FA and WB received consulting honoraria and travel grant from BioMarin.TF received grant from BioMarin, Ultragenyx and Alexion.PFCS received consulting honoraria and travel grant from Pfizer, Novo Novordisk, Merck, BioMarin and Sandoz.PFVM received consulting honoraria from BioMarin, research fellowship from Ultragenyx and travel grant from BioMarin and Ultragenyx.JL received consulting honoraria and travel grant from BioMarin and Sanofi-Genzyme.DC, ARB, NTR, FC, MCHR and CML declare no conflict of interest. All fees received by CML are donated to the CML Medical Foundation for Research and Genetic Diagnosis Support for families with unknown genetic disorders.