Document is current
Any future updates will be listed below
-
Authors
O’Leary, Claire
Forte, Gabriella
Mitchell, Nadia L.
Youshani, Amir Saam
Dyer, Adam
Wellby, Martin P.
Russell, Katharina N.
Murray, Samantha J.
Jolinon, Nelly
Jones, Simon A
Stacey, Kevin
Davis, Daniel M.
Henckaerts, Els
Palmer, David N.
Kamaly-Asl, Ian
Bigger, Brian W.
-
Funding
Funding for this research was provided by:
Jonah’s Just Begun, (Improving brain delivery of adeno-associated gene therapy vectors for the treatment of MPS IIIC)
- License Information
-
More Information
Article History
Received: 24 February 2023
Accepted: 15 May 2023
First Online: 5 July 2023
Declarations
:
: All experimental protocols were approved by the Lincoln University Animal Ethics Committee (Lincoln University Animal Ethics applications 213 and 423).
: Delivery of HGSNAT using AAV to MPSIIIC is the subject of a patent held by BB, COL and EH. BB is a consultant and grant holder for AVROBIO, Orchard Therapeutics and Phoenix Nest. BB and COL received payments from Phoenix Nest for previous MPSIIIC work.
