Modelling Gaucher disease progression: long-term enzyme replacement therapy reduces the incidence of splenectomy and bone complications
Crossref DOI link: https://doi.org/10.1186/s13023-014-0112-x
Published Online: 2014-07-24
Published Print: 2014-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
van Dussen, Laura
Biegstraaten, Marieke
Dijkgraaf, Marcel GW
Hollak, Carla EM
License valid from 2014-07-24
Article History
Received: 2 November 2013
Accepted: 4 July 2014
First Online: 24 July 2014