Establishing medical plausibility in the context of orphan medicines designation in the European Union
Crossref DOI link: https://doi.org/10.1186/s13023-014-0175-8
Published Online: 2014-12-05
Published Print: 2014-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Tsigkos, Stelios
Mariz, Segundo
Llinares, Jordi
Fregonese, Laura
Aarum, Stiina
Frauke, Naumann-Winter
Westermark, Kerstin
Sepodes, Bruno
License valid from 2014-12-01