Compassionate use of orphan drugs
Crossref DOI link: https://doi.org/10.1186/s13023-015-0306-x
Published Online: 2015-08-21
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Hyry, Hanna I.
Manuel, Jeremy
Cox, Timothy M.
Roos, Jonathan C. P.