Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years’ treatment
Crossref DOI link: https://doi.org/10.1186/s13023-015-0338-2
Published Online: 2015-09-29
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Kampmann, Christoph
Perrin, Amandine
Beck, Michael