Evaluation of pre-symptomatic nitisinone treatment on long-term outcomes in Tyrosinemia type 1 patients: a systematic review
Crossref DOI link: https://doi.org/10.1186/s13023-017-0696-z
Published Online: 2017-09-11
Published Print: 2017-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Geppert, Julia
Stinton, Chris
Freeman, Karoline
Fraser, Hannah
Clarke, Aileen
Johnson, Samantha
Sutcliffe, Paul
Taylor-Phillips, Sian
Funding for this research was provided by:
UK National Screening Committee