Received: 29 November 2017
Accepted: 15 February 2018
First Online: 23 February 2018
Ethics approval and consent to participate
: The studies reviewed herein were designed and conducted in compliance with the ethical principles of Good Clinical Practice guidelines in accordance with the Declaration of Helsinki. Investigators obtained informed written consent from each patient and/or parent or guardian before study participation. The study protocols and the informed consent forms were reviewed and approved by the ethics committees/institutional review boards for each study and at each study site.
: Not applicable.
: Ari Zimran was a consultant for Protalix BioTherapeutics during the course of the taliglucerase alfa studies and has received honoraria from Genzyme/Sanofi, Pfizer, and Shire; his current institution, the Gaucher Clinic, receives grant/research support from Genzyme/Sanofi and Shire. Michael Wajnrajch and Betina Hernandez are employees of Pfizer Inc. Gregory M. Pastores received grant/research support from Actelion, Alexion, Amicus/GSK, BioMarin, Genzyme/Sanofi, Protalix BioTherapeutics/Pfizer, and Shire.
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