Text and Data Mining valid from 2018-09-10
Received: 18 May 2018
Accepted: 29 August 2018
First Online: 10 September 2018
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: Not applicable.
: LN and AH are employees of Sanofi Genzyme. MH and PS, employees of Mapi at the time this study was conducted, were paid consultants to Sanofi Genzyme. AM is a Professor and Clinical Director at Lysosomal Storage Disorders Unit, Department of Haematology, Royal Free Hospital.
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