Poelman, E.
Hoogeveen-Westerveld, M.
van den Hout, J. M. P.
Bredius, R. G. M.
Lankester, A. C.
Driessen, G. J. A.
Kamphuis, S. S. M.
Pijnappel, W. W. M.
van der Ploeg, A. T. http://orcid.org/0000-0002-3359-1324
Funding for this research was provided by:
Prinses Beatrix Spierfonds (project number W.OR13-21, W.OR15-10, W.OR16-07)
Ministerie van Economische Zaken (no number available)
Stichting Vrienden van het Sophia (project number S17-32)
Metakids (project number 2016-063)
Conselho Nacional de Desenvolvimento Científico e Tecnológico (no number available)
Colciencias (no number available)
Genzyme (no number available)
Article History
Received: 2 October 2018
Accepted: 28 February 2019
First Online: 22 March 2019
Ethics approval and consent to participate
: All procedures followed were in accordance with the ethical standards of the responsible committee on human experimentation (institutional and national) and with the Helsinki Declaration of 1975, as revised in 2000. All patients and/or their parents provided informed consent. The medical ethical committee of the Erasmus MC approved the study protocol.
: Not applicable.
: AvdP and JvdH have provided consulting services for various industries in the field of Pompe disease under an agreement between these industries and Erasmus MC, Rotterdam, the Netherlands. The other authors declare that they have no conflict of interest.
: Springer Nature remains neutral with regard to jurisdictional claims in published maps and institutional affiliations.