Received: 26 August 2020
Accepted: 16 November 2020
First Online: 30 November 2020
Ethics approval and consent to participate
: Parental consent was obtained to use the patients’ medical data, photographs, and videos.
: Parental consent was obtained to publish the patient’s medical data, photographs, and videos.
: Can Ficicioglu, MD, PhD, has served as an advisor or consultant for: Genzyme, Horizon, Orphan Tech., Recordati, Shire, and Sobi. He received grants for clinical research from: Genzyme, Orphan Tec, RegenxBio, Takeda, and Vtesse. Dena R. Matalon, MD, none. Nicole Luongo, PA-C, none. Caitlin Menello, CGC,, none. Tracy Kornafel,, none. Andrew J. Degnan, MD, none.