Funding for this research was provided by:
National MPS Society (2014)
National Center for Advancing Translational Sciences (UL1TR002494)
National Institute of Diabetes and Digestive and Kidney Diseases (R01DK072124-01A3)
National Cancer Institute (R01CA113930-01A1)
Text and Data Mining valid from 2020-03-17
Received: 28 August 2019
Accepted: 7 February 2020
First Online: 17 March 2020
Ethics approval and consent to participate
: All procedures performed in studies involving human participants were in accordance with the ethical standards of the authors’ institutional research committees. This study was approved by the Institutional Review Board of CHOC Children’s Specialists (IRB # 131107) and Saint Louis University (IRB # 24454), and complied with the standards of the 1964 Declaration of Helsinki and current ethical guidelines.
: All patients or their parents consented to publication of clinical, biochemical, and molecular details.
: The authors declare that they have no competing interests.