Funding for this research was provided by:
Received: 26 October 2020
Accepted: 1 February 2021
First Online: 12 February 2021
Ethics approval and consent to participate
: All study procedures were in accordance with ethical standards of the 1964 Helsinki Declaration and its later amendments, relevant laws, institutional guidelines, and approved by an institutional review board. Participant informed consent (written or verbal) was obtained as approved by the institutional review board.
: Not applicable.
: CG and CD are employees of Orphazyme A/S. TS, MP, LLP, HD, CB, MC, and EM declare no competing interests.