Giugliani, Roberto http://orcid.org/0000-0001-9655-3686
Barth, Anneliese Lopes
Dumas, Melissa Rossi Calvão
da Silva Franco, José Francisco
de Rosso Giuliani, Liane
Grangeiro, Carlos Henrique Paiva
Horovitz, Dafne Dain Gandelman
Kim, Chong Ae
de Araújo Leão, Emilia Katiane Embiruçu
de Medeiros, Paula Frassinetti Vasconcelos
Miguel, Diego Santana Chaves Geraldo
Moreira, Maria Espírito Santo Almeida
dos Santos, Helena Maria Guimarães Pimentel
da Silva, Luiz Carlos Santana
da Silva, Luiz Roberto
de Souza, Isabel Neves
Nalin, Tatiele
Garcia, Daniel
Funding for this research was provided by:
Ultragenyx Farmacêutica Brasil LTDA
Article History
Received: 9 March 2021
Accepted: 14 May 2021
First Online: 22 May 2021
Declarations
:
: The ethical approval of this study is covered by the MPS Brazil Network project (#03 066/GPPG/HCPA). Consent for publication was obtained from all participants/caregivers.
: All the patients or caregivers gave written informed consent to this publication.
: RG, PFM, JFF have received speaker honoraria from Ultragenyx Farmacêutica Brasil LTDA. JFF, RG, PFM and LRS served as clinical investigators for one study sponsored by Ultragenyx Pharmaceutical Inc. ALB, MRD, LRG, CHG, DDGH, CAK, EKEL, DSM, MEM, HPS, LCSS and INS report no conflicts of interest. TN and DG are employees of Ultragenyx Farmacêutica Brasil LTDA and hold stock in Ultragenyx Pharmaceutical Inc.