De Amicis, Ramona http://orcid.org/0000-0003-0403-5465
Baranello, Giovanni
Foppiani, Andrea
Leone, Alessandro
Battezzati, Alberto
Bedogni, Giorgio
Ravella, Simone
Giaquinto, Ester
Mastella, Chiara
Agosto, Caterina
Bertini, Enrico
D’Amico, Adele
Pedemonte, Marina
Bruno, Claudio
Wells, Jonathan C.
Fewtrell, Mary
Bertoli, Simona
Funding for this research was provided by:
Fondazione Telethon (GUP15014)
Famiglie SMA (grant 2015)
Article History
Received: 28 May 2021
Accepted: 24 August 2021
First Online: 4 September 2021
Declarations
:
: The study was approved by the Ethics Committee of the University of Milan (n.7/16), accepted by the other institutional partners and complied following the Helsinki declaration. The parents, on behalf of their children, gave their written informed consent to the study.
: Not applicable.
: Some authors (EB, CA, CB, AD, MP) are members of the European Reference Network for Neuromuscular Diseases (ERN EURO-NMD). GiBa has received speaker and consultancy honoraria from AveXis, Inc., Roche, PTC, and Sarepta Therapeutics, but he received no funding for this specific study. All the other authors have no conflicts of interest relevant to this article to disclose.