Mistry, P. K. http://orcid.org/0000-0003-3447-6421
Kishnani, P.
Wanner, C.
Dong, D.
Bender, J.
Batista, J. L.
Foster, J.
Article History
Received: 29 July 2022
Accepted: 4 September 2022
First Online: 17 October 2022
Declarations
:
: All patients provided informed consent to participate in the Registries.
: Not applicable.
: PKM has received research and travel support from Sanofi. PK has received research/grant support from Sanofi and Amicus Therapeutics, has received consulting fees and honoraria from Sanofi, Amicus Therapeutics, Maze Therapeutics, JCR Pharmaceutical and Asklepios Biopharmaceutical, Inc. (AskBio), is a member of the Pompe and Gaucher Disease Registry Advisory Board for Sanofi, Amicus Therapeutics, and Baebies, and has equity in Asklepios Biopharmaceutical, Inc. (AskBio), which is developing gene therapy for Pompe disease and Maze Therapeutics, which is developing a small molecule in Pompe disease. CW has received honoraria for board meetings and lecturing from Amicus, Chiesi, Idorsia, Sanofi, and Takeda. JB, JLB, DD, JF are employees of Sanofi and may hold Sanofi stocks.