Lachmann, Robin H. http://orcid.org/0000-0002-2618-2581
Diaz, George A.
Wasserstein, Melissa P.
Armstrong, Nicole M.
Yarramaneni, Abhimanyu
Kim, Yong
Kumar, Monica
Funding for this research was provided by:
Sanofi Genzyme (Sanofi Genzyme)
Article History
Received: 14 December 2022
Accepted: 6 April 2023
First Online: 25 April 2023
Declarations
:
: Local Institutional Review Boards (IRB) at both study sites approved the protocol (corresponding author’s IRB: Health Research Authorities London Bridge Research Ethics Committee; reference 13/LO/1522) and patients/parents provided written informed consent prior to patient screening. All clinical data were de-identified. The study adhered to the principles set out in the Declaration of Helsinki.
: Not applicable.
: RHL, MPW, and GAD have received consulting fees, honoraria and travel support to attend scientific meetings from Sanofi.NA, AY, YK, and MK are employees of Sanofi and may own Sanofi stock.