Pession, Andrea
Di Rocco, Maja
Venturelli, Francesco http://orcid.org/0000-0002-7133-3713
Tappino, Barbara
Morello, William
Santoro, Nicola
Giordano, Paola
Filippini, Beatrice
Rinieri, Simona
Russo, Giovanna
Girardi, Katia
Ruggiero, Antonio
Galea, Eulalia
Antonucci, Roberto
Tovaglieri, Nicola
Porta, Fulvio
Tartaglione, Immacolata
Giona, Fiorina
Fagioli, Franca
Burlina, Alberto
Mura, Rosamaria
Russo, Bambina
Tornesello, Assunta
Menna, Giuseppe
Russo, Delia
Caniglia, Maurizio
Schettini, Sergio
Onofrillo, Daniela
Ladogana, Saverio
Civino, Adele
,
Funding for this research was provided by:
Sanofi
Article History
Received: 24 September 2022
Accepted: 4 June 2023
First Online: 16 June 2023
Declarations
:
: The study was approved by the ethical review committee of the coordinating center “Comitato Etico Indipendente dell’Azienda Ospedaliero Universitaria di Bologna, Policlinico s.Orsola-Malpighi” (Protocol number 2060/2015) and subsequently by all participating centers, before the enrolment of any patient. Informed consent was obtained from all parents or legal representatives of the children included in the study.
: Not applicable.
: AP received honoraria from BioMarin Pharmaceutical Inc, Dicopharm, PTC Therapeutics, and Sanofi for participation at advisory boards and speaking at their sponsored meetings. MDR received travel support and honoraria from Sanofi and Takeda. WM received travel grants and honoraria from Sanofi-Genzyme for speaking at sponsored meetings. NS receives honoraria from NOVARTIS and AMGEN for participation at advisory boards and speaking at their sponsored meetings. PG received honoraria from Bayer Roche Sobi for participation at advisory board. GR receives honoraria from NOVARTIS, AMGEN, GRIFOLS and BIOVALLEY for participation at advisory boards and speaking at their sponsored meetings. FG receives honoraria from Sanofi and Takeda for participation at advisory boards and speaking at their sponsored meetings. FF receives honoraria from Jazz Pharmaceutical, Dicopharm, Bayer, Takeda and Sanofi for participation at advisory boards and speaking at their sponsored. AB receives honoraria for advisory boards and speaking at their sponsored meetings from Takeda, BioMarin Pharmaceutical Inc, PTC Therapeutics, Sanofi-Genzyme. FP received honoraria by BIOTEST, TILLOMED, JAZZ, TAKEDA, CHIESI for participations to advisory boards and sponsored meetings. FV, BT, SR, KG, AR, EG, RA, NT, BF, IT, RM, BR, AT, GM, DR, MC, SS, DO, SL, AC have no conflicts of interest to disclose.