Kishnani, Priya S. http://orcid.org/0000-0001-8251-909X
Kronn, David
Suwazono, Shugo
Broomfield, Alexander
Llerena, Juan
Al-Hassnan, Zuhair Nasser
Batista, Julie L.
Wilson, Kathryn M.
Periquet, Magali
Daba, Nadia
Hahn, Andreas
Chien, Yin-Hsiu
Funding for this research was provided by:
Sanofi
Article History
Received: 20 April 2023
Accepted: 18 November 2023
First Online: 6 December 2023
Declarations
:
: Legal guardians of all patients provided informed written consent to submit their health information to the Registry, to be used for further analysis and data sharing; independent registry sites are responsible for ensuring this compliance. The Registry protocol, informed consent form, and any locally required authorization documents are reviewed and approved by the local fully constituted Institutional Review Board or Independent Ethics Committee.
: Not applicable.
: Priya S. Kishnani: Advisory Board: Amicus, Baebies, Sanofi; Consulting Fees: Amicus, AskBio, Sanofi, Vertex, Maze therapeutics. Contracted Research: Amicus, Sanofi, Valerion. Honoraria: Amicus, AskBio, Sanofi, Vertex. Ownership Interest less than 5% (stocks, stock options or other ownership interest excluding diversified mutual funds): AskBio, Baebies. Travel Expenses: Amicus, Sanofi. David Kronn: Advisory Board: AskBio and Sanofi; Contracted research: Sanofi; Speaker’s bureau: Sanofi; Travel expenses: AskBio and Sanofi. Shugo Suwazono: Advisory board: Sanofi. Alexander Broomfield: Advisory board: Sanofi and Honoraria: Orchard Therapeutics and Sanofi. Juan Llerena: Advisory Board: Sanofi, Biomarin; Consulting Fees: Sanofi, Biomarin; Travel expenses: Sanofi, Biomarin. Zuhair Nasser Al-Hassnan: Advisory board: Sanofi. Andreas Hahn: Advisory board: Sanofi and Amicus Therapeutics; Honoraria and consulting fees: Sanofi, Amicus, Takeda, Avrobio, and Biomarin. Yin-Hsiu Chien: Advisory board: Amicus Therapeutics and Sanofi, Contracted research: Sanofi, Honoraria, and consulting fees from Sanofi. Kathryn M. Wilson: contractor for Navitas Data Sciences, funded by Sanofi. Julie L. Batista, Nadia Daba, and Magali Periquet: employees of Sanofi may hold shares and stock options.