Article History
Received: 18 October 2023
Accepted: 3 February 2024
First Online: 19 February 2024
Declarations
:
: RegistrAME is approved by the ethics committee (CEIm): Hospital Universitario 12 de Octubre Committee approval No CEIm: 20/413. All participants provided their informed consent.
: Not applicable.
: ET has received grant support to conduct studies by Ionis/Biogen and Roche. Serves as consultant of Avexis, Novartis, Biogen, Roche, Cytokinetics, Biologix, PTC. MdL has offered advisory support to Roche in the development of risdiplam. MGC has received support from Roche for attendance to scientific congresses.