Singh, Rani H. http://orcid.org/0000-0003-2096-2592
Bourdages, Marie-Hélène
Kurtz, Angela
MacLoed, Erin
Norman, Chelsea
Ratko, Suzanne
van Calcar, Sandra C.
Kenneson, Aileen
Funding for this research was provided by:
Recordati Rare Diseases (N/A)
Article History
Received: 8 November 2023
Accepted: 30 March 2024
First Online: 18 April 2024
Declarations
:
: The Human Research Ethics Boards of the following institutions reviewed the protocol and either approved it or deemed it exempt from review: Emory University School of Medicine, Children’s University Hospital of Quebec, Mount Sinai, Children’s National Medical Center, University of Utah, London Health Sciences Centre, and Oregon Health & Science University. Each institution waived the requirement for informed consent.
: Not applicable.
: The authors declare that they have no competing interests.