Truninger, Moritz Ilan http://orcid.org/0000-0001-6724-5019
Werner, Helene http://orcid.org/0000-0002-7081-7695
Landolt, Markus Andreas http://orcid.org/0000-0003-0760-5558
Hahn, Andreas
Hennermann, Julia B.
Lagler, Florian B.
Möslinger, Dorothea
Pfrimmer, Charlotte
Rohrbach, Marianne
Huemer, Martina http://orcid.org/0000-0002-0590-678X
Funding for this research was provided by:
Sanofi (Sanofi)
Article History
Received: 1 May 2024
Accepted: 18 September 2024
First Online: 28 September 2024
Declarations
:
: The study was approved by the review boards of all participating hospitals and conducted in full accordance with the Declaration of Helsinki. Participants gave informed consent for their and their child’s participation. Adolescent patients gave informed consent for participation.
: Not applicable.
: The authors declare that they have no financial interests or personal relationships that could have influenced the conduct or reporting of this research. MH has received unrestricted research grants from Nutricia Metabolics and SOBI, and consultancy honoraria or travel support from Aeglea, Nutricia Metabolics, Sanofi, Recordati, and Immedica Pharma, all unrelated to this work. AH has received consulting fees, honoraria, and/or travel expenses from Amicus, Takeda, and Sanofi. JBH has received consulting fees, honoraria, and/or travel expenses from Chiesi, Amicus, Takeda, and Sanofi. FBL has received unrestricted research grants from Sanofi, Takeda, and Chiesi, and honoraria as speaker and consultant from these companies and from Biomarin and Amicus. These relationships pose no conflict of interest with the current study.