Deimmunization for gene therapy: host matching of synthetic zinc finger constructs enables long-term mutant Huntingtin repression in mice
Crossref DOI link: https://doi.org/10.1186/s13024-016-0128-x
Published Online: 2016-09-06
Published Print: 2016-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Agustín-Pavón, Carmen
Mielcarek, Michal
Garriga-Canut, Mireia
Isalan, Mark
Funding for this research was provided by:
European Research Council (641232, 201249)
Wellcome Trust (102944)