Concolino, Daniela
Deodato, Federica
Parini, Rossella
Article History
First Online: 16 November 2018
Ethics approval and consent to participate
: Not applicable.
: Not applicable.
: RP participated as principal investigator in the phase III trial for ERT in MPS IVA (BioMarin) and has recently participated as subinvestigator to the phase I/II trial for intrathecal ERT in MPS IIIA (Shire). RP has received honoraria for consulting or speaking engagement from BioMarin, Sanofi Genzyme, SOBI, and Shire. DC has received honoraria for speaking engagements from Shire and Sanofi Genzyme. FD has received honoraria for speaking engagements from Sanofi Genzyme and Shire.
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