Gragnaniello, Vincenza
Deodato, Federica
Gasperini, Serena
Donati, Maria Alice
Canessa, Clementina
Fecarotta, Simona
Pascarella, Antonia
Spadaro, Giuseppe
Concolino, Daniela
Burlina, Alberto
Parenti, Giancarlo
Strisciuglio, Pietro
Fiumara, Agata
Casa, Roberto Della
Article History
Received: 26 September 2021
Accepted: 22 January 2022
First Online: 5 March 2022
Declarations
:
: A.B.: was/is a member of Scientific Advisory Boards and received honoraria from Genzyme, Biomarin, Nutricia, APR, PIAM, Takeda, Recordati Rare Diseases; A.F.: financial support for University Research Grants by Sanofi-Genzyme; guest and travel expenses for National and International congresses by Takeda, Sanofi Genzyme and Biomarin; A.P.: none; C.C.: none; D.C.: none; F.D.: none; G.P.: none; G.S.: none; M.A. Donati: none; P.S.: none; R.D.C.: none; S.F.: none; S.G.: declares travel grants and consulting fees from Genzyme Sanofi; V.G.: none.