Successful switch from enzyme replacement therapy to miglustat in an adult patient with type 1 Gaucher disease: a case report
Crossref DOI link: https://doi.org/10.1186/s13256-016-1060-y
Published Online: 2016-11-08
Published Print: 2016-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Giuffrida, Gaetano
Lombardo, Rita
Di Francesco, Ernesto
Parrinello, Laura
Di Raimondo, Francesco
Fiumara, Agata
License valid from 2016-11-08