Received: 24 August 2020
Accepted: 29 September 2020
First Online: 3 November 2020
Ethics approval and consent to participate
: Not applicable.
: Written informed consent for publication of their clinical details was obtained from the patients.
: The Division of Pediatric Endocrinology and Diabetes at Ulm University Medical Center participated as a study centre in the therapy studies RM-493-014 and RM-493-022 funded by Rhythm Pharmaceuticals Inc. All authors are part of the study team.