Funding for this research was provided by:
the Lorenzo-Piaggio Foundation
Received: 12 June 2019
Accepted: 30 June 2020
First Online: 16 July 2020
Ethics approval and consent to participate
: Eligible subjects were included in the study only after providing written informed consent. Ethics approval has been obtained from the local Ethics Committee (EKNZ 2015–221) and the National Swiss Drug Agency (Swissmedic, Reference number: 2016DR2067).
: We confirm that (1) the authors of this manuscript had access to all study data, are responsible for all contents of the manuscript, and had authority over the preparation of the manuscript and the decision to submit the manuscript for publication and (2) all authors have read and approved the submission of this manuscript to the journal.
: DF is principle investigator for studies on spinal muscular atrophy sponsored by Hofmann-La Roche Ltd. There are no other activities related to commercial companies. The authors declare that they have no competing interests.