Audhya, Ivana F.
Szabo, Shelagh M. http://orcid.org/0000-0002-9044-3192
Bever, Andrea
O’Sullivan, Fiona
Malone, Daniel C.
Feeny, David
Neumann, Peter
Iannaccone, Susan T.
Jayasinghe, P.
Gooch, Katherine L.
Funding for this research was provided by:
Sarepta Therapeutics
Article History
Received: 31 March 2023
Accepted: 6 December 2023
First Online: 15 December 2023
Declarations
:
: Ethical approval for this study was obtained through Advarra IRB, and all participants provided informed consent prior to participation.
: Not applicable.
: This study was funded by Sarepta Therapeutics, Inc. IFA and KLG are employees of Sarepta Therapeutics, Inc. SMS, AB, FOS and PJ are employees of Broadstreet HEOR, which received funds from Sarepta to conduct this study. DF, PN, and DCM received consulting fees related to this work. DF has a proprietary interest in Health Utilities Incorporated, Dundas, Ontario, Canada. HUInc. distributes copyrighted Health Utilities Index (HUI) materials and provides methodological advice on the use of HUI. STI has received research funding or consulting fees from Avexis, Biogen, Fibrogen, Mallinkrodt, Regeneron, Sarepta, Scholar Rock, PTC Therapeutics, Pfizer, MDA, CureSMA, NIH, Genentech-Roche, and BCBS.