Rio, Paula
Baños, Rocio
Lombardo, Angelo
Quintana‐Bustamante, Oscar
Alvarez, Lara
Garate, Zita
Genovese, Pietro
Almarza, Elena
Valeri, Antonio
Díez, Begoña
Navarro, Susana
Torres, Yaima
Trujillo, Juan P
Murillas, Rodolfo
Segovia, Jose C
Samper, Enrique
Surralles, Jordi
Gregory, Philip D
Holmes, Michael C
Naldini, Luigi
Bueren, Juan A
Funding for this research was provided by:
European Union (FP7 GA 222878 PERSIST)
European Commission (HEALTH‐F5‐2012‐305421)
European Regional Development FEDER Funds
ERC (249845 TARGETINGGENETHERAPY)
Italian Ministry of Health
Spanish Ministry of Economy and Competitiveness (PLE 2009/0100)
Spanish Ministry of Economy and Competitiveness (SAF 2009‐07164)
Spanish Ministry of Economy and Competitiveness (SAF 2012‐39834)
Fondo de Investigaciones Sanitarias
Instituto de Salud Carlos III (RETICS‐RD06/0010/0015)
Instituto de Salud Carlos III (RD12/0019/0023)
Dirección General de Investigación de la Comunidad de Madrid (S2010/BMD‐2420)
La Fundació Privada La Marató de TV3 (121430/31/32)
Generalitat de Catalunya (SGR0489‐2009)
Marató de TV3 (464/C/2012)
Spanish Ministry of Science and Innovation (SAF2012‐31881)
Article History
Received: 9 August 2013
Revised: 16 April 2014
Accepted: 17 April 2014
First Online: 23 May 2014
Conflict of interest
: P.D.G. and M.C.H. are current or former employees of Sangamo BioSciences, Inc. The rest of the authors declare that they have no conflict of interest.