Soria, Leandro R https://orcid.org/0000-0002-7124-856X
Gurung, Sonam
De Sabbata, Giulia
Perocheau, Dany P https://orcid.org/0000-0001-5450-8801
De Angelis, Angela
Bruno, Gemma
Polishchuk, Elena
Paris, Debora
Cuomo, Paola
Motta, Andrea
Orford, Michael
Khalil, Youssef https://orcid.org/0000-0001-9025-3017
Eaton, Simon
Mills, Philippa B
Waddington, Simon N
Settembre, Carmine https://orcid.org/0000-0002-5829-8589
Muro, Andrés F https://orcid.org/0000-0002-9628-0494
Baruteau, Julien https://orcid.org/0000-0003-0582-540X
Brunetti‐Pierri, Nicola https://orcid.org/0000-0002-6895-8819
Funding for this research was provided by:
Fondazione Telethon
Ministero dell'Istruzione, dell'Università e della Ricerca
NIHR Great Ormond Street Hospital
UKRI | Medical Research Council (MR/T008024/1)
Innovate UK Biomedical Catalyst (14720)
Nutricia Metabolic Research Grant
London Advanced Therapy (2CiC017)
Article History
Received: 22 July 2020
Revised: 23 November 2020
Accepted: 25 November 2020
First Online: 28 December 2020
Conflict of interest
: The authors declare no that they have no conflict of interest.