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Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity

Crossref DOI link: https://doi.org/10.15252/emmm.202113968

Published Online: 2021-12

Published Print: 2022-01-11

Update policy: https://doi.org/10.1002/crossmark_policy

Authors

Eggers, Michelle https://orcid.org/0000-0001-5387-2118
Vannoy, Charles H https://orcid.org/0000-0003-3617-8081
Huang, Jianyong

Purushothaman, Pravinkumar

Brassard, Jacqueline https://orcid.org/0000-0002-3305-3163
Fonck, Carlos

Meng, Hui

Prom, Mariah J

Lawlor, Michael W

Cunningham, Justine

Sadhu, Chanchal

Mavilio, Fulvio https://orcid.org/0000-0003-0459-4320
Funding

Funding for this research was provided by:

Audentes Therapeutics
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Publication History

Received: 2021-01-14

Accepted: 2021-11-09

Published: 2021-12-01