Coratti, Giorgia http://orcid.org/0000-0001-6666-5628
Pane, Marika
Brogna, Claudia
Ricotti, Valeria
Messina, Sonia
D’Amico, Adele
Bruno, Claudio
Vita, Gianluca http://orcid.org/0000-0003-4190-8042
Berardinelli, Angela
Mazzone, Elena
Magri, Francesca
Ricci, Federica
Mongini, Tiziana
Battini, Roberta
Bello, Luca
Pegoraro, Elena
Baranello, Giovanni
Previtali, Stefano C. http://orcid.org/0000-0003-2546-4357
Politano, Luisa http://orcid.org/0000-0002-0925-7158
Comi, Giacomo P.
Sansone, Valeria A.
Donati, Alice
Hogrel, Jean Yves
Straub, Volker http://orcid.org/0000-0001-9046-3540
De Lucia, Silvana
Niks, Erik http://orcid.org/0000-0001-5892-5143
Servais, Laurent
De Groot, Imelda
Chesshyre, Mary
Bertini, Enrico
Goemans, Nathalie http://orcid.org/0000-0002-5157-7155
Muntoni, Francesco
Mercuri, Eugenio http://orcid.org/0000-0002-9851-5365
,
Funding for this research was provided by:
Fondazione Telethon (GUP 15011)
Association Française contre les Myopathies (IMDEX/ NCT02780492)
NIHR Great Ormond Street Hospital Biomedical Research Centre